uniQure's AMT-130 Receives FDA's Fast Track Designation for Huntington's Disease
Shots:
- The FDA’s FT designation follows P-I/II study assessing AMT-130 in patients with Huntington’s disease with an expected initiation in H2’19
- FDA grant Fast Track designation to facilitate the development & and expedite the review of drugs to treat serious conditions and fill an unmet medical need
- AMT-130 is an AVV5 gene therapy one-time administered carrying a DNA cassette encoding a microRNA that non-selectively lowers or knocks-down human huntingtin protein and targets highly toxic exon1 protein fragment
Ref: uniQure | Image: Twitter
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